Vertex präsentiert positive Langzeitdaten zu CASGEVY™ (exagamglogene autotemcel) auf der Jahrestagung und Ausstellung der American Society of Hematology (ASH) und gibt Programmupdate bekannt.
About Transfusion-Dependent Beta Thalassemia (TDT) TDT is a rare, genetic blood disorder that requires regular blood transfusions to survive. Patients with TDT have a reduced life expectancy and often face significant complications from the disease and its treatment, including iron overload from transfusions and organ damage. Current treatment options for TDT are limited and often … Weiterlesen